Gene Therapy


  • Housing and breeding programs for transgenic lines
  • Experience with administration of various client’s test articles for multiple
    gene therapy methods e.g. CRISPR, AAV, Oligo, mRNA, RNAi, siRNA,
    ceDNA, antisense
  • Proficient in multiple routes of administration of test materials for gene therapy
  • Multiple tissue collections according to client requests
  • Established and developed in-vitro assays to assess the efficiency of the
    gene therapy treatments e.g. ammonia, hEPO, FIX, FVIII, PHE, luciferase
  • Evaluate test compound toxicity by clinical observations and laboratory
    test e.g. liver enzymes


Routes of Administration

  • Intravenous
  • Hydrodynamic intravenous
  • Subcutaneous
  • Oral gavage
  • Intramuscular
  • Nebulization
  • Intravitreal
  • Intrathecal
  • Intratracheal
  • Intraarticular
  • Intranasal
  • Intracerebral ventricular


  • Experience with multiple transgenic strains
  • Proficient with multiple dose administration methods
  • Established various in-vitro assays
  • IVIS imaging capabilities

Our global liaison team paves the way to extended resources, abundant pharmacology models and budget friendly options seamlessly.